#genetherapy

6 days of hard work. Wonderful progress. And another step forward for Erik. 💚 We have just completed Erik’s second DMI intensive, and once again I’m amazed by what he can achieve with the right therapy, the right support and someone who truly believes in his potential. A huge thank you to @martha_seibel_karacsonyi for bringing DMI into Erik’s life and for challenging him, encouraging him and helping him discover what his little body is capable of. What you are giving him feels truly life-changing to us. ❤️ This time, the vest has been a real game changer too. It gives Erik the additional support he needs to work stronger and for longer during his sessions — allowing him to practice movements, build strength and push himself that little bit further. Watching this video makes me incredibly emotional. Things that may look like small movements to others are huge victories for Erik. Every time he holds himself a little stronger, controls his body a little better or manages something he couldn’t do before, it gives us so much hope. Once again, we spent six intensive days working, pushing and celebrating every little achievement. And the progress has been wonderful to see. Thank you, Martha, for your dedication, your energy and for believing in Erik. 💚 We are so grateful to be able to do these intensives with you at @therapiestelle in Buchs. And a huge thank you also to @clarapoif, Erik’s physiotherapist at home, for all the continuous work she does with him between intensives, helping him build strength and keep progressing every week. ❤️ Now some well-deserved rest — and we’ll be back in October for the next intensive! 💪 One step at a time. One new possibility at a time. ❤️ #DMI #Physiotherapy #RareDisease #ASNSD #nevergiveup

Unlocking the Future: What is Gene Therapy? 🧬 Discover how scientists are rewriting DNA to treat and even cure genetic disorders! #GeneTherapy #Genetics #Science #STEM

Meet Federico Mingozzi, PhD, a leading expert in #genetherapy working on groundbreaking advancements for #cysticfibrosis. Dr. Mingozzi's team is developing non-viral delivery technologies, like lipid nanoparticles, to deliver genetic therapies directly to cells—offering hope to the final 10% of the #CF community still waiting for breakthroughs. His work is not only a major leap for CF but could also impact genetic therapies for other diseases. 🎥 Learn more at the link in our bio! Thank you to our 2025 #CFAwarenessMonth Tier 2 sponsors—@viatrisinc, @baxter_intl, @recodetx, @boehringer_ingelheim, and 4D Molecular Therapeutics—for supporting our #SciencEE series and helping us to #CrossOutCF for good!

YES. THE mRNA VACCINES ARE GENE THERAPY. But fears around its known dangers caused officials to deny it! SCANDALOUS!! In this interview, you’ll also hear: • Why he believes public health leaders “knew the truth and lied” • The role of LNPs (lipid nanoparticles) and unintended systemic distribution • How vaccine-induced myocarditis has been misunderstood • Why Gov censorship ruined trust in public health 🎙 Full interview with Dr. Robert Redfield — now live on The Dana Parish Podcast! #GeneTherapy #mRNAVaccine #Censorship #LNPContamination #DrRobertRedfield #TheDanaParishPodcast #PublicHealthCrisis #VaccineTransparency #ScienceAccountability #MedicalFreedom mRNA | gene editing | covid shots | vaccine risks | spike protein | myocarditis | censorship | public health | informed consent | pandemic response

💛✨ C’est avec une immense fierté que j’ai présenté hier la conférence de presse du #Telethon2025 👸🏼 Avec comme marraine, une artiste engagée, sensible et déterminée… @jesuissanta999 est une femme en OR ! 💛 Bravo à toute la famille @telethon_france #laurencethiennotherment @emmanuelled18 @steph_scuzoim 💌 Merci de votre confiance à la team @yannickletranchant @eve.demumieux @marysemarascia @a_lesaunier1953 📺 Rdv les 5 et 6 décembre prochains sur les antennes de @francetelevisions cette 39e édition 🍀 Pour Noé, Paulin, Maxence, Lucie et tous les autres, soyez au rendez-vous ! #NeRienLacher 💓Sans oublier mes bonnes fées @carine_torrent @televisionstyle @delphinedelafosse @sylpricoiff . . #telethon #telethongaming #téléthon #maladie #maladiegenetique #genetherapy #recherche #scientifique #genetique #essaiclinique #traitement #medicament #espoir #dons #famille #enfant #solidarite #generosite #ensemble #toujoursycroire

Meet Mattijs Bulcaen, PhD (@mattijsbulcaen), a rising trailblazer in the field of gene editing and genome engineering for #cysticfibrosis. Dr. Bulcaen and his team are using cutting-edge technologies to precisely correct the genetic mistakes that cause #CF, offering new hope for the final 10% of the CF community. His work, combined with the spirit of perseverance from Emily's Entourage, push the boundaries of what's possible. 🎥 Learn more at the link in our bio. Thank you to our 2025 #CFAwarenessMonth Tier 2 sponsors—@viatrisinc, @baxter_intl, @recodetx, @boehringer_ingelheim, and 4D Molecular Therapeutics—for supporting our #SciencEE series and helping us to #CrossOutCF!

𝐈𝐭 𝐰𝐚𝐬 𝐚𝐧 𝐡𝐨𝐧𝐨𝐮𝐫 𝐭𝐨 𝐰𝐞𝐥𝐜𝐨𝐦𝐞 𝐇.𝐄. 𝐎𝐧𝐮𝐫 𝐒̧𝐚𝐲𝐥𝐚𝐧, 𝐂𝐨𝐧𝐬𝐮𝐥 𝐆𝐞𝐧𝐞𝐫𝐚𝐥 𝐨𝐟 𝐓𝐮𝐫𝐤𝐞𝐲, 𝐭𝐨 𝐌𝐞𝐝𝐜𝐚𝐫𝐞 𝐑𝐨𝐲𝐚𝐥 𝐒𝐩𝐞𝐜𝐢𝐚𝐥𝐭𝐲 𝐇𝐨𝐬𝐩𝐢𝐭𝐚𝐥. He visited our Gene Therapy Unit and met some of the parents who travelled from Turkey for their children’s treatment under my care. I’m truly grateful for his kind words, support, and encouragement. His visit meant a lot to all of us. T.C. Dubai Başkonsolosu Sayın Onur Şaylan’ı Medcare Royal Speciality Hospital’da ağırlamak benim için bir onurdu. Gen Tedavi Ünitemizi ziyaret etti ve Türkiye’den gelen ve tedavileri benim gözetimimde devam eden bazı ailelerle görüştü. Destekleyici sözleri ve teşvikleri için kendisine içtenlikle teşekkür ederim. Ziyareti hepimiz için çok kıymetliydi. #genetherapy #genetherapyuae #genetherapyinturkey #TurkeyHealthcare #PediatricCare #turkey #peadiatricneurology #drvivekmundada #medcareroyalhospital

What is #genetherapy 🧬 #health #science

#DYK: In recent years, gene therapy has emerged as a revolutionary one-time approved treatment option for those with hemophilia B? This treatment aims to enable people with hemophilia B to create their own clotting factor, potentially delivering bleed protection that lasts years without ongoing, regular infusions. Those in the U.S. can learn more about this groundbreaking approach at www.portraitsofprogress.com. #genetherapy #DrivenByOurPromise

جین تھراپی کی مدد سے تھیلیسیمیا کے مرض کا کامیاب علاج #ExpressNews #BreakingNews #LatestUpdates #LatestNews #GeneTherapy #Thalassemia

She’s one tough cookie is our Piglet! 🥹🥰 #zolgensma #genetherapy #spinalmuscularatrophy #smatype1 #mama

This week, I had the privilege of conducting a strategic engagement visit to the headquarters of @Caring_Cross in Gaithersburg, Maryland, in continuation of the collaboration formalised between the @WellbeingAfrica Foundation and Caring Cross through our recently signed Memorandum of Understanding. Grounded in a shared mission to democratise access to life-saving biotherapeutics, including CAR-T cell and gene therapies, for conditions that continue to burden communities across Nigeria, such as cancer, sickle cell disease, and HIV, I was pleased to engage with Dr. Boro Dropulić and the Caring Cross team to advance our shared implementation agenda. Caring Cross is a pioneering non-profit that exemplifies how innovation, ethics, and equity can converge to redefine the future of global health. Their decentralised manufacturing model for advanced therapies, empowering local hospitals and clinical centres to produce and administer treatments on-site, is deeply aligned with WBFA’s commitment to strengthening Nigeria’s health systems from within. Through this engagement, I witnessed firsthand the technological rigour, scientific stewardship, and values-based leadership driving Caring Cross’s efforts. Our dialogue reaffirmed the pressing need to synchronise policy, regulatory frameworks, capacity-building, and public trust to ensure that 21st-century cures can be delivered sustainably in Nigeria. As Founder-President of the Wellbeing Foundation Africa, I reiterated our commitment to ensuring that this collaboration serves as a global exemplar, as we aim not only to introduce transformative treatments into Nigeria’s health landscape but to do so with a steadfast commitment to inclusivity, safety, and community ownership. I extend my deep appreciation to Dr. Boro and his remarkable team for their visionary work and their trust in Nigeria’s capacity to lead in this critical space. United in purpose, we are shaping a future in which diagnosis no longer signals despair, but rather access, dignity, and wellbeing. #WBFACaringCross  #GeneTherapy #WellbeingForAll